- CONTACT US
- AFS
- Business
- Bussiness
- Car
- Career
- Celebrity
- Digital Products
- Education
- Entertainment
- Fashion
- Film
- Food
- Fun
- Games
- General Health
- Health
- Health Awareness
- Healthy
- Healthy Lifestyle
- History Facts
- Household Appliances
- Internet
- Investment
- Law
- Lifestyle
- Loans&Mortgages
- Luxury Life Style
- movie
- Music
- Nature
- News
- Opinion
- Pet
- Plant
- Politics
- Recommends
- Science
- Self-care
- services
- Smart Phone
- Sports
- Style
- Technology
- tire
- Travel
- US
- World

WASHINGTON (AP) — The Food and Drug Administration said Friday it will add a new warning and other limitations to a gene therapy for Duchenne’s muscular dystrophy that's been linked to two patient deaths.
The infused therapy from Sarepta Therapeutics will carry a boxed warning — the most serious type — alerting doctors and patients to the risk of potentially fatal liver failure with the treatment, the FDA said in a release.
The one-time therapy, Elevidys, has been under FDA scrutiny since the company reported the first of two deaths of teenage boys in March. Following a second death reported in June, the FDA briefly called for halting all shipments of the drug. But the agency quickly reversed course after facing pushback from patient families and libertarian activists close to President Donald Trump.
Elevidys is the first U.S.-approved gene therapy for Duchenne’s muscular dystrophy, a fatal muscle-wasting disease that affects boys and young men.
In addition to the boxed warning, the FDA is also limiting the drug's approved use to patients who are 4 years old and up and can still walk. Previously the FDA had allowed the drug's use in immobile patients, who generally have more advanced disease.
New labeling will also recommend weekly liver function monitoring for the first three months of treatment, as well as other precautionary steps.
Elevidys is Sarepta's best-selling product and recent headwinds against the drug have weighed heavily on the company and its stock. In July, the Cambridge, Massachusetts-based company announced it would lay off 500 employees.
Sarepta Therapeutics Inc. shares rose 7.7% in trading after the FDA announcement, reflecting improved visibility for investors about the company's outlook.
___
The Associated Press Health and Science Department receives support from the Howard Hughes Medical Institute’s Department of Science Education and the Robert Wood Johnson Foundation. The AP is solely responsible for all content.
LATEST POSTS
- 1
Israel violated ceasefire with Hezbollah more than 10,000 times, UNIFIL claims - 2
Report in relation to renaming Herzog Park set to be withdrawn - 3
Bismuth’s haredi draft bill won’t change enlistment, IDI expert tells 'Post' - 4
I work with companies to confront addiction in the workplace. The hidden crisis is costing corporate America millions. - 5
German police 'cleared path for fascists with batons,' protesters say
FDA adds strongest warning to Sarepta gene therapy linked to 2 patient deaths
Bayer reports positive results for blood thinner after 2023 setback
Amazon sued over 'punitive' handling of employee absences
Consumers advised to dispose of 19 cooking pans due to lead leaching risk, FDA reports
Shah Capital pushes for Novavax sale, warns of proxy fight
November Lease Deals for the 2025 Kia EV6 are Too Good to Pass Up
Toyota Motor Europe to roll out smart EV charging through new partnerships
Merck sees over $5 billion opportunity in Cidara's experimental flu drug
Cyber Monday 2025: Save over 70% on HBO Max with this Prime Video streaming deal













